New Developments in Gene Therapy for Muscular Dystrophy

These live interactive Webinars will discuss gene therapy approaches in the management of muscular dystrophies.


Program length (60 minutes)

  • Welcome and Introduction
  • Rationale for and Approaches to Gene Therapy
  • Understanding the Different Approaches to Gene Therapy and the Associated Challenges
  • Discussion and Audience Question and Answer Session


Date / Time
Event Details


Richard S. Finkel, MD

Professor of Neurology
University of Central Florida College of Medicine
Division Chief, Pediatric Neurology
Nemours Children's Hospital
Orlando, Florida


Professor of Neurology
Johns Hopkins School of Medicine
Director, Center for Genetic Muscle Disorders
Kennedy Krieger Institute
Baltimore, Maryland

Goal Statement
The goal of this activity is to improve the knowledge and competence of learners in the rationale and the use of gene therapy approaches for patients with muscular dystrophies.

Target Audience 
This program is intended for pediatricians, pediatric neuromuscular specialists, general neuromuscular specialists, nurse practitioners, nurses, and other healthcare providers who care for patients with muscular dystrophy.

Learning Objectives
Upon completion of this activity, participants should be able to:

  • Describe the rationale for gene therapy based on the underlying molecular basis of different muscular dystrophies
  • Discuss the mechanisms of gene therapy
  • Assess recent evidence on approved and emerging therapies for muscular dystrophy
  • Cite the challenges associated with gene therapy approaches to treating and curing muscular dystrophies


Joint Accreditation Statement

In support of improving patient care, Clinical Care Options, LLC (CCO) is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC) to provide continuing education for the healthcare team.

Physician Continuing Medical Education

Credit Designation 

CCO designates this live activity for a maximum of 1.0 AMA PRA Category 1 Credit™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

Disclosure of Conflicts of Interest
Clinical Care Options, LLC (CCO) requires instructors, planners, managers, and other individuals who are in a position to control the content of this activity to disclose any relevant conflict of interest (COI) they may have as related to the content of this activity. All identified COI are thoroughly vetted and resolved according to CCO policy. CCO is committed to providing its learners with high-quality CME/CE activities and related materials that promote improvements or quality in healthcare and not a specific proprietary business interest of a commercial interest.